The Next Chapter star Leah Messer opens up about navigating protecting her daughter Ali amid her muscular dystrophy diagnosis ...

Top-line Phase 3 trial data show ambulatory boys with Duchenne continued with motor improvements two years after a single ...

Johnny Quintana’s life changed at the age of 19 when he was diagnosed with a rare form of muscular dystrophy called ...

Teen Mom star Leah Messer admits it’s “very challenging” helping daughter Aliannah “balance” her desire for freedom with the ...

The gene therapy improved motor functions in children with Duchenne muscular dystrophy two years after treatment ...

The Muscular Dystrophy Association (MDA) has selected Lily Sander from Charlotte, North Carolina, as its 2025 MDA National ...

Roche and Sarepta Therapeutics have shared positive top-line results from a late-stage study of Elevidys (delandistrogene ...

MDA launches 75th Anniversary campaign and premieres new public service announcement (PSA) to mark 75 years of impact in the ...

Sidra Medicine, a member of Qatar Foundation, has established a gene therapy centre to treat rare genetic diseases such as ...