Congenital Adrenal Hyperplasia, Congenital Hypothyroidism, thalassemia, cystic fibrosis, and Severe Combined ImmunoDeficiency (SCID). Newborn screening uses noninvasive hearing tests, pulse ...
The FDA has granted priority review designation for two new drug applications for a selective corticotropin-releasing factor type 1 receptor to treat congenital adrenal hyperplasia, according to a ...