What a gene therapy win means for the Huntington’s disease pipeline

“Beyond UniQure, the pipeline includes highly promising approaches that will ideally move the goal from merely managing ...

Exposure to any germs could've killed her. 11 years later, she's living a normal life thanks to a gene therapy treatment.

New research found that gene therapy for children with a form of severe combined immunodeficiency was successful in 95% of ...
News Medical on MSN

Gene therapy shows long-term success in children with rare immune disorder

Results from the largest cohort of children who received a gene therapy for a rare immunodeficiency condition have shown the ...

New gene therapy shows promise in preventing kidney disease in type 1 diabetes

A new gene therapy approach aimed at protecting people with type 1 diabetes from developing diabetic kidney disease—a serious ...

Gene therapy delivers lasting immune protection in children with rare disorder

An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...
Managed Healthcare Executive

Outcomes Model Is Starting With Gene Therapy for Sickle Cell Disease

Managed Healthcare Executive gives C-suite executives in health plans and provider organizations news and strategies for ...
Morningstar

Biologic Competition, Payer Pressures, and Gene Therapy Momentum Define a Pivotal Moment in nAMD and DME Management, According to Spherix Global Insights

Exton, Pennsylvania, July 10, 2025 (GLOBE NEWSWIRE) -- Recently released research from Spherix Global Insights provides a timely look at the increasingly competitive and complex treatment landscape ...