A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain ...

Faulty versions of the LMNA gene can cause a wide range of health problems, including heart muscle disease (dilated ...

Results from the largest cohort of children who received a gene therapy for a rare immunodeficiency condition have shown the ...

Gene therapy is at the cutting edge of medicine, with exciting new products being developed and used to treat a wide variety of genetic diseases. However, one major roadblock to delivering gene ...

For more than a decade, the strongest AIDS drugs could not fully control Matt Chappell's HIV infection. Now his body controls it by itself, and researchers are trying to perfect the gene editing that ...

While resurrected animal species grab headlines, Colossal’s behind-the-scenes R&D may be poised to make an impact for humans ...

Researchers have developed a novel delivery system for sending CRISPR reagents to brain cells, where they perform their gene editing function. In this approach, a nanoparticle exposes cells to the ...

Sound waves at frequencies above the threshold for human hearing are routinely used in medical care. Also known as ultrasound ...

A revolutionary gene-silencing technique has shown that a single treatment can dramatically lower LDL cholesterol levels for over a year—without permanently altering DNA. Could this be the future of ...