New research found that gene therapy for children with a form of severe combined immunodeficiency was successful in 95% of ...
A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain ...
In a study published in Nature Medicine, Leone and her team reported the first targeted gene therapy to restore myelin, the ...
1hon MSN
Longevity gene from supercentenarians offers hope for disease that causes rapid aging in children
A new breakthrough in a rare genetic disease which causes children to age rapidly has been discovered using 'longevity genes' ...
Scientists have reversed diabetic heart failure with a genetic therapy in mice and miniature human "hearts" grown from stem ...
The MCO-010 vector uses surviving cells in the retina to produce a photosensitive protein that may help patients regain some ...
Abeona Therapeutics Inc. (Nasdaq: ABEO), a commercial-stage biopharmaceutical company developing cell and gene therapies for ...
Researchers have achieved the first demonstration in mice of using gene therapy to reverse hallmark symptoms of SYNGAP1-related disorder, a devastating condition affecting an estimated 1 million ...
Results from MUSIC-HFpEF Phase 1/2a clinical trial show favorable safety profile and early clinical benefits with SRD-002 gene therapy BOSTON, May 19, 2025 (GLOBE NEWSWIRE) -- Medera Inc. (“Medera”), ...
Smarter design through targeted delivery and human-relevant testing can save the industry from costly safety failures.
Jesse Gelsinger died after receiving a gene therapy treatment to treat a liver disease. The death sparked an investigation ...
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