The drug’s accelerated approval was based on the intermediate endpoint of improvement in knee extensor muscle strength. The ...

(Reuters) -Danish drugmaker Novo Nordisk and Omeros have signed a licensing deal worth up to $2.1 billion for the U.S.-based ...

BioCryst Pharmaceuticals said on Tuesday it would buy Astria Therapeutics in a cash-and-stock deal valued at about $700 ...

In May, a historic moment in science and medicine was captured in a single photo that circulated across news outlets ...

Having already established a commercial infrastructure for its oral hereditary angioedema (HAE) drug Orladeyo and eager to ...

Bristol Myers Squibb's acquisition of Orbital Therapeutics includes OTX-201, a next-gen CAR T-cell therapy, and a proprietary ...

Working with agency partner DCX Growth Accelerator, GeneDX takes direct aim at the issue of underdiagnosis of pediatric rare diseases.

But recently, scientists took inspiration for such a super drug from a quiet corner of the medical world: The small subset of ...

Nine-year-old Emma D. of Fishers, Indiana, received national recognition for her courage this week at the American Kidney ...

Stevie Ringel is the founder of the Kizuna Foundation, an organization seeking a treatment for a genetic retinal mutation ...