Holding back tears, Christine Ulrich recalls how her daughter Veda once loved dancing, drawing and babbling. Now, she can no longer speak or even hold a crayon. Three years ago, Veda was diagnosed ...

Not everyone is given equal opportunities in life, but even when faced with the most difficult challenges, it’s not the circumstances that define us, but our outlook. Logan was born in 2007 alongside ...

As a pediatrician, I’ve dedicated my career to advocating for children’s health. But when my daughter, Eliza, was diagnosed with Sanfilippo syndrome, a fatal childhood neurological disease, I realized ...

MUSKEGO, Wis. - Muskego parents were given a life-changing diagnosis. Their 3-year-old girl has a rare genetic disorder with no cure, but the family is not giving up hope. They're asking for your help ...

As parents watch their kids transition from infancy into childhood, it’s common to look for signs of progressing development. Are they sleeping through the night? Can they remember new words and use ...

Denali Therapeutics Inc. DNLI announced that the FDA has extended its review timeline of the Biologics License Application ...

The effects of Sanfilippo syndrome in small children are so devastating that the rare disease is often known as "childhood dementia." About one in 70,000 newborns inherit this disorder. The affected ...

COMMERCE TWP., Mich. (WXYZ) — As we celebrate the holidays with our families it's important to remember the small blessings many of us take for granted. Whether it ...

COLUMBUS, Ohio — Growing up, Clark Willmore always dealt with a curved back and was "a little clumsy," according to his dad Japeth. His family decided to take Clark to the doctor to learn more about ...

DelveInsight’s, “Sanfilippo Syndrome - Pipeline Insight, 2025” report provides comprehensive insights about 8+ companies and 10+ pipeline drugs in Sanfilippo Syndrome pipeline landscape. It covers the ...