More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...
Type 3 and 4 are typically for the older age groups. And type 4 is mainly in the adult onset. They do have the ability to walk. However, over time, they may lose their ability to walk and will ...
one of the diseases that is being researched is Spinal Muscular Atrophy. It’s a disease that people are born with that affects babies and adults. It is estimated that in the state of Idaho ...
A man with a muscle-wasting disease is pleased Manitoba is asking a federal agency to reconsider its opposition to a ...
"We are working with urgency to deliver the potentially transformative benefits of apitegromab to children and adults with ...
Scholar Rock submitted its BLA of apitegromab for the treatment of patients with Spinal Muscular Atrophy with a request for Priority Review to be given. Explore more details here.
An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines ...
The health activists argue that the government is empowered with effective law and policy tools and therefore should ...
Health activists demand government action to reduce the cost of SMA medicines, citing constitutional obligations and ...
Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...
In a good-news-bad-news week for Biogen, the company will cut an undisclosed number of employees, just as a higher dose of ...