Problems with chemical messengers like dopamine were tied to posture issues in SMA in a mouse study, but levodopa therapy may ease symptoms.

"Novartis’ Phase III spinal muscular atrophy therapy trial meets primary endpoint" was originally created and published by Clinical Trials Arena, a GlobalData owned brand. The information on ...

Topline data were announced from a phase 3 trial evaluating intrathecal onasemnogene abeparvovec (OAV101 IT), an investigational gene therapy ... 18 years with spinal muscular atrophy (SMA ...

Novartis has shared positive top-line results from a late-stage study of its investigational gene therapy in patients aged two to less than 18 years with the rare neuromuscular disease spinal muscular ...

Back to Healio Topline results from a phase 3 clinical trial showed an investigational gene therapy for young people with spinal muscular atrophy type 2 increased mobility and slowed disease ...

More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...

The mutation that causes Spinal Muscular Atrophy (SMA) can be detected in a prenatal screen. But a parent's decision to test for this terrible disease is not as easy as you would think.

and physical and occupational therapists, who develop exercise programs and assistive strategies to enhance mobility and daily living skills. Spinal Muscular Atrophy (SMA) is a significant ...

Family meet for children with spinal muscular atrophy (SMA) held at IMCH, Kozhikode, with therapy, exhibition, and medical ...