Scholar Rock submitted its BLA of apitegromab for the treatment of patients with Spinal Muscular Atrophy with a request for Priority Review to be given. Explore more details here.

A man with a muscle-wasting disease is pleased Manitoba is asking a federal agency to reconsider its opposition to a ...

An investigational higher dose of spinal muscular atrophy drug nusinersen gains attention as the FDA and European Medicines ...

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Scholar Rock (SRRK), a late-stage biopharmaceutical company developing innovative treatments for spinal muscular atrophy, ...

Find Spinal Muscular Atrophy Sma Latest News, Videos & Pictures on Spinal Muscular Atrophy Sma and see latest updates, news, information from NDTV.COM. Explore more on Spinal Muscular Atrophy Sma .

Health activists demand government action to reduce the cost of SMA medicines, citing constitutional obligations and ...

The health activists argue that the government is empowered with effective law and policy tools and therefore should ...

Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...

Asher Cantrell, diagnosed with SMARD 1, has received experimental gene therapy after social media support and is currently ...

Thiruvananthapuram: The Kerala government is planning to launch a registry for rare diseases and set up a treatment clinic in ...