Beacon Therapeutics may have found a guiding light in a disease area where other companies have stumbled with its laruparetigene zovaparvovec (laru-zova), a gene therapy that proved early improvements ...

A Johnson & Johnson gene therapy in development for an inherited vision-loss disorder has failed a Phase 3 study, the latest clinical research setback for a rare eye disease that so far has no ...

Many genetic variants linked to inherited eye disorders rarely lead to disease, meaning up to 2% of people could carry these variants without ever developing vision problems, according to a new s tudy ...

Genetic diseases are a compelling target for viral gene therapy, but the results can be spotty at best. There's good news, though. On Wednesday, researchers presented evidence from a breakthrough gene ...

The results call into question how faulty genes wind up causing diseases, researchers said TUESDAY, Dec. 23, 2025 (HealthDay News) — Genetics aren’t necessarily destiny for those with mutations ...