Treatment introduces an expansion of the scope of gene therapies that might lead to similar treatments for neurodegenerative ...

The gene therapy company uniQure has announced top-level data from its trial of AMT-130, a new gene therapy designed to treat Huntington’s disease. Globally, an estimated 4.88 per 100,000 people ...

After the deaths of three patients, the maker of an investigational gene therapy stopped shipments of the drug after it refused a request from the U.S. Food and Drug Administration (FDA) to pull the ...

Shattuck Labs, Inc. ( NASDAQ: STTK) The United European Gastroenterology (UEG) Congress UEG Week 2025 October 8, 2025 10:00 AM EDT ...

Physiology or medicine was the third prize area Alfred Nobel mentioned in his will laying out his wishes for the Nobel Prize.

In the mood for a horror movie this Halloween but don't feel like being terrified by what you're watching? Here are 15 ...

These ten hilarious comedy movie scenes are often overlooked, but they deserve more appreciation for their humor and should be discussed more overall.

Researchers announce breakthrough results for AMT-130, the first disease-modifying treatment for Huntington's disease, with ...

Researchers in the UK say clinical trials conducted on a small number of people show that a new gene therapy has slowed the progression of Huntington's disease, a fatal neurological condition. The ...

Drugmaker Pfizer Inc said on Tuesday that it had administered doses of its experimental gene therapy for rare degenerative muscular condition Duchenne muscular dystrophy (DMD) to an additional 9 boys, ...

An experimental gene therapy was found to slow the progression of Huntington’s disease in a “pivotal” Phase 1/2 study, according to drugmaker uniQure, marking a major step toward a potential first ...

Genetic deficiency of otoferlin, a protein critical to synaptic transmission by the sensory hair cells of the ear, causes congenital deafness. Medicines to treat the condition are lacking; ...