These results are what we hoped for when we first began developing this approach,' one researcher said. View on euronews ...

Results from the largest cohort of children who received a gene therapy for a rare immunodeficiency condition have shown the ...

Since 2019, MIT researchers have published a new concept called prime editing, which is more precise than regular CRISPR-Cas9 gene editing. As a result, it has fewer off-target effects and less chance ...

New research found that gene therapy for children with a form of severe combined immunodeficiency was successful in 95% of ...

Medication has long been the cornerstone of treatment for people with epilepsy, but it doesn't stop seizures for everyone and ...

Faulty versions of the LMNA gene can cause a wide range of health problems, including heart muscle disease (dilated ...

The Xevo CDMS enhances analysis of large biomolecules, crucial for next-gen therapeutics, using individual-particle mass measurement for molecules up to 150+ MDa. Electrostatic Linear Ion Trap (ELIT) ...

A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain ...

Treatments for cancer are continuously improving, but they can still cause debilitating, even fatal, side effects.