New research found that gene therapy for children with "bubble boy disease," or SCID, was successful in 95% of trial ...
An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...
Despite announcing a broad pivot to siRNA earlier this year, Sarepta is following through with an investigational gene ...
News-Medical.Net on MSN
Experimental gene therapy restores immune system function in children with genetic immune disorder
An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...
An experimental gene therapy has successfully treated dozens of children with a rare and fatal immune disorder, a promising ...
News Medical on MSN
Gene therapy shows long-term success in children with rare immune disorder
Results from the largest cohort of children who received a gene therapy for a rare immunodeficiency condition have shown the ...
In a study published in Nature Medicine, Leone and her team reported the first targeted gene therapy to restore myelin, the ...
Researchers convert type A kidney to type O, potentially reducing wait times and saving lives. Experimental gene therapy ...
A novel, validated seven-gene transcriptomic signature can predict TNF inhibitor response in patients with rheumatoid ...
With a new COO and several consultants that were formerly as Spark Therapeutics, CorriXR plans on "rewriting the rules of ...
Stevie Ringel is the founder of the Kizuna Foundation, an organization seeking a treatment for a genetic retinal mutation ...
A new breakthrough in a rare genetic disease which causes children to age rapidly has been discovered using ‘longevity genes’ ...
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