New research found that gene therapy for children with a form of severe combined immunodeficiency was successful in 95% of ...
This article outlines common CMC problems that are obstacles that steal momentum and create costly detours in the development ...
News-Medical.Net on MSN
Experimental gene therapy restores immune system function in children with genetic immune disorder
An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...
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Longevity gene from supercentenarians offers hope for disease that causes rapid aging in children
A new breakthrough in a rare genetic disease which causes children to age rapidly has been discovered using 'longevity genes' ...
Researchers from the University of Bristol and IRCCS MultiMedica showed that a gene linked to supercentenarians’ longevity ...
News-Medical.Net on MSN
CRISPR therapy shows promise against influenza in human lung chips
The Influenza A virus (IAV) has been the cause of six major flu pandemics, responsible for 50 to 100 million deaths globally.
Key takeawaysA blood stem cell gene therapy co-developed by UCLA's Dr. Donald Kohn restored immune function in 59 of 62 children with ADA-SCID, a rare ...
In a study published in Nature Medicine, Leone and her team reported the first targeted gene therapy to restore myelin, the ...
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Health Rounds: Scientists change kidney blood type, a potential advance for transplant recipients
Researchers convert type A kidney to type O, potentially reducing wait times and saving lives. Experimental gene therapy ...
A new study offers hope for brain cancer patients facing memory loss from radiotherapy. By blocking a single immune receptor, ...
A new breakthrough in a rare genetic disease which causes children to age rapidly has been discovered using ‘longevity genes’ ...
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