The US Food and Drug Administration (FDA) has approved SpringWorks Therapeutics’ Gomekli (mirdametinib) to treat ...

The firm says Gomekli’s approval comes 17 days earlier than the FDA action date “with a clearly differentiated label” relative to AstraZeneca’s (AZN) Koselugo for adult and pediatric patients with ...

Adam Pearson used his neurofibromatosis struggles to succeed in acting and advocacy, inspiring others to accept differences ...

The kinase inhibitor is now approved for adults and children aged ≥ 2 years with neurofibromatosis type 1 who have unresectable symptomatic plexiform neurofibromas.

Cupid's Undie Run sent dozens of half-naked runners through Saturday to raise awareness for a genetic disease.

Tuesday, the agency signed off on SpringWorks’ Gomekli (mirdametinib) as a treatment for the rare genetic disorder ...

The Food and Drug Administration (FDA) approved a new drug to treat a disorder causing the growth of non-cancerous tumors on ...

The U.S. Food and Drug Administration said on Tuesday it has approved SpringWorks Therapeutics' drug to treat a type of rare ...

A Jacksonville woman pens a letter of gratitude to actor Sebastian Stan for his recent words on normalizing disfigurement and ...

The FDA's green light for GOMEKLI is a significant achievement for SpringWorks, especially as it comes with a rare pediatric disease priority review voucher, which could be valued at around $100 ...

The Food and Drug Administration approved mirdametinib, brand name Gomekli, from SpringWorks Therapeutics (SWTX), a kinase inhibitor, for adult ...

You might see some skimpily dressed people running through downtown Cleveland today. The Cupid's Undies Run is back, raising money to fight Neurofibromatosis.