The evolution of functional assessments for spinal muscular atrophy (SMA) highlights the challenges of adapting pediatric ...

The US Food and Drug Administration has approved a new drug application for a tablet version of Evrysdi (risdiplam) for people living with spinal muscular atrophy (SMA).

Spinal muscular atrophy (SMA) is a debilitating genetic condition that’s usually fatal by a few years of age. But an ...

Exercise can make a significant difference for patients with SMA by working alongside other medical advancements to improve ...

Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth. Scientists at St. Jude Children's Research Hospital led the first in uterotreatment of SMA with ...

February 19, 2025) Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth. Scientists ...

February is Rare Disease Awareness month. The upcoming week has been declared Rare Disease Awareness week, with Rare Disease ...

The MDA Let's Play online community will celebrate its fifth anniversary in March 2025, and will engage in the MDA Shamrocks ...

Composer Ari Kinarthy, who has a rare genetic condition called Spinal Muscular Atrophy, is the subject of Ari’s Theme, ...

The FDA has approved Evrysdi in tablet form for patients with spinal muscular atrophy aged 2 years and older who weigh more ...

With so many holidays, awareness days, education weeks, and heritage months happening all year long, we’ve been slowly ...