Results from the largest cohort of children who received a gene therapy for a rare immunodeficiency condition have shown the ...
New research found that gene therapy for children with a form of severe combined immunodeficiency was successful in 95% of ...
An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has ...
A new gene therapy approach aimed at protecting people with type 1 diabetes from developing diabetic kidney disease—a serious ...
“Beyond UniQure, the pipeline includes highly promising approaches that will ideally move the goal from merely managing ...
A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain ...
Fifteen-year-old Dominic Juillette, a Grade 10 student at Fort St. James Secondary School, was born with a genetic defect that caused night blindness. But a cutting-edge surgery using retinal gene ...
Woody Guthrie (1912–1967) was a well-known singer/songwriter with undiagnosed Huntington's disease (HD), born to a family burdened by undiagnosed HD. Guthrie’s mother, Nora, had the disease and was ...
AUSTIN (KXAN) — An exceptionally rare and fatal genetic disease may finally have a solution. Huntington’s Disease affects one in ten to twenty thousand Americans. The disease is a mixture of dementia ...
Gene therapy is being used to treat Huntington's disease and is proving to be effective. Trump Makes Announcement Against Taliban NFL World Was in Disbelief After Adonai Mitchell's Mistake Erased a ...
An experimental gene therapy was found to slow the progression of Huntington's disease in a "pivotal" Phase 1/2 study, according to drugmaker uniQure, marking a major step toward a potential first ...
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