Gene Therapy: Revolutionizing Medicine By Tackling Diseases At Their Genetic Roots
Gene therapy represents a paradigm shift in modern medicine, offering unprecedented opportunities to combat diseases at their ...
US FDA approves SpringWorks' genetic disorder drug
The U.S. Food and Drug Administration said on Tuesday it has approved SpringWorks Therapeutics' drug to treat a type of rare ...
KOIN Portland on MSN1d
Portugal. The Man highlight rare disease month as bandmember’s daughter battles genetic disease
February is Rare Disease Month, an annual effort to highlight the challenges families can face while navigating rare ...
Can Your Child Inherit Rare Disorders? Know Why Genetic Intervention Is Important
Your genes play a huge role in what makes and shapes your entire existence. Since you inherit your genes from your parents, ...
FDA approves new genetic disorder drug
The Food and Drug Administration (FDA) approved a new drug to treat a disorder causing the growth of noncancerous tumors on ...
The Brighterside of News on MSN1d
Researchers find genetic link between heart disease and brain development
Congenital heart disease (CHD) affects approximately 1% of live births. Thanks to surgical advancements, infants born with ...
FiercePharma2d
Amid takeover talk, SpringWorks scores FDA nod for rare genetic disease treatment Gomekli
Tuesday, the agency signed off on SpringWorks’ Gomekli (mirdametinib) as a treatment for the rare genetic disorder ...
The Conversation4d
Sickle cell disease is a genetic disorder that causes lifelong suffering – here’s what you need to know
In the UK, approximately 17,500 people have sickle cell disease and 300 babies are born with the condition each year. It is a genetic disorder caused by inherited mutations in a person’s DNA ...
West Africans have a high risk of kidney disease – new study confirms genetic cause
Our study thus confirmed what was found in people of African descent in the US: the genetic origin underpinning the excess ...
Genetic map identifies 1,000 potential kidney disease treatment targets
More than 1,000 genes may serve as possible treatment targets for individuals with kidney disease, according to a new study, ...
Daily Mail12d
I got two brain tumours and skin cancer twice before I was 18 years old due to a rare genetic disorder - but I'm not letting that hold me back
A teenager was diagnosed with skin cancer and a brain tumour four times before she turned 18 after discovering she had a rare genetic disorder. Ruby-Jo Sneed discovered she had a rare genetic ...
WESA8d
Pitt researchers find spinal stimulation restored muscles wasted by rare genetic disorder
Three patients with spinal muscular atrophy had improved muscle strength and could walk farther after a month of daily spinal ...