The kinase inhibitor is now approved for adults and children aged ≥ 2 years with neurofibromatosis type 1 who have ...
The US Food and Drug Administration has approved mirdametinib for the treatment of neurofibromatosis type 1 (NF1) in adults ...
Adam Pearson used his neurofibromatosis struggles to succeed in acting and advocacy, inspiring others to accept differences ...
Adult and pediatric patients with neurofibromatosis type 1 who have symptomatic plexiform neurofibromas that are not amenable ...
Gomekli is the second ever FDA-approved treatment for rare tumor disease, NF1-PN and the first to be approved for both adult ...
Approval makes Gomekli the first treatment to be approved for both adults and pediatric patients for neurofibromatosis type 1 ...
The FDA on Tuesday signed off on SpringWorks Therapeutics’ mirdametinib—now to carry the brand name Gomekli—for the treatment ...
The US Food and Drug Administration (FDA) has approved SpringWorks Therapeutics’ Gomekli (mirdametinib) to treat ...
Cupid's Undie Run sent dozens of half-naked runners through Saturday to raise awareness for a genetic disease.
The Pittsburgh Auto Show will be on Friday, Saturday, Sunday and Monday at the David L. Lawrence Convention Center downtown.
Runners are encouraged to strip down to their underwear or don creative costumes to raise awareness and money for NF with ...
Nemcic is far from alone. Robert Krouse is a former DOD contractor who said he worked alongside these vets. He endured two cancers, having 80% of his tongue removed along with his vocal cords and all ...