Adam Pearson used his neurofibromatosis struggles to succeed in acting and advocacy, inspiring others to accept differences ...

The US Food and Drug Administration has approved mirdametinib for the treatment of neurofibromatosis type 1 (NF1) in adults ...

Adult and pediatric patients with neurofibromatosis type 1 who have symptomatic plexiform neurofibromas that are not amenable ...

The US Food and Drug Administration (FDA) has approved SpringWorks Therapeutics’ Gomekli (mirdametinib) to treat ...

Gomekli is the second ever FDA-approved treatment for rare tumor disease, NF1-PN and the first to be approved for both adult ...

Cupid's Undie Run sent dozens of half-naked runners through Saturday to raise awareness for a genetic disease.

Runners are encouraged to strip down to their underwear or don creative costumes to raise awareness and money for NF with ...

Reno will take to the streets in just their undies during Cupid’s Undie Run. The event raises awareness of neurofibromatosis ...

GOMEKLI is the first and only medicine approved for both adults and children with NF1-PN –– Approval based on positive data ...

Sophia Watson is in urgent need of life-saving treatment for a tumor, but an insurance dispute has left her family without coverage.