News Medical on MSN1d
First prenatal treatment for spinal muscular atrophy shows promising results
Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth. Scientists at St. Jude Children's Research Hospital led the first in uterotreatment of SMA with ...
Macleans.ca1d
How Patients Living With Spinal Muscular Atrophy Can Achieve More Through Active Living
Exercise can make a significant difference for patients with SMA by working alongside other medical advancements to improve ...
Olean Times Herald2dOpinion
Some rare diseases not as rare as you think
February is Rare Disease Awareness month. The upcoming week has been declared Rare Disease Awareness week, with Rare Disease ...
Armed robbery in Revesby2d
First Prenatal Spinal Muscular Atrophy Therapy Shows Promise
February 19, 2025) Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth. Scientists ...
manilatimes3d
Muscular Dystrophy Association Launches Nation's Largest St. Patrick's Day Fundraising Campaign Celebrating 75 Years of Progress
The MDA Let's Play online community will celebrate its fifth anniversary in March 2025, and will engage in the MDA Shamrocks ...
Documentary Ari's Theme shines light on power of music therapy
Composer Ari Kinarthy, who has a rare genetic condition called Spinal Muscular Atrophy, is the subject of Ari’s Theme, ...
pharmaphorum2d
SMA Awareness Month: How pharma and digital solutions can improve patient care
Spinal Muscular Atrophy (SMA) is a rare disease affecting ... for which life expectancy is less than 18 months without treatment. This SMA Awareness month, we look at how digital health solutions ...
What a $2 million per dose gene therapy reveals about drug pricing
Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...