A case report described an infant with concurrent HDFN and SMA who was succesfully treated with an onasemnogene abeparvovec ...

Sales growth driven by continued strong performance from Entresto (+31% cc), Cosentyx (+25% cc), Kesimpta (+49% cc), Kisqali (+49% cc), Pluvicto (+42% cc) and Leqvio (+114% cc) Core operating income ...

Background: Spinal and bulbar muscular atrophy (SBMA) or Kennedy disease [OMIM ... consent form and allowed anonymised publication of their clinical information and photos. The study included all ...

The 18-month-old, suffering from a rare genetic disease called Spinal Muscular Atrophy (SMA ... the scalpel after a gap of two years. Dr HD Ranganath, Congress MLA from Kunigal ...

In a LinkedIn post, Monisha shared the challenges of travelling with her 14-year-old daughter, Keya, who has Spinal Muscular Atrophy (SMA). Understanding the early signs, potential complications ...

A Boston-area biopharmaceutical firm has submitted a biologics license application to the FDA for its investigational, fully ...

Three patients with spinal muscular atrophy had improved muscle strength and could walk farther after a month of daily spinal ...

A new drug-free, minimally invasive intervention targets the root cause of progressive loss of neural function in spinal muscle atrophy (SMA), an inherited neuromuscular disease.

who are living with Spinal Muscular Atrophy (SMA) with the support of her mother, sister and teacher. Ms. Keya was felicitated by the Visakha Rasagna Vedika, a cultural organisation, at the Public ...