Patients with ATTR-CM had significantly impaired global longitudinal strain and higher mechanical dispersion compared to their first-degree relatives who were not affected by the disease. Increased ...

Getty Images A post-hoc analysis of the ATTRibute-CM trial showed that acoramidis significantly improves survival in patients with p.V142I ATTRv-CM. By Month 30, the risk of combined all-cause ...

Of the 33,829 blood donors analyzed, only 179 were D negative (0.53%). This finding complements existing studies on the relative rarity of this blood type in Asia. Among East and Southeast Asian ...

The levels of NT-proBNP, left ventricular mass index, maximal wall thickness, and E/E′ ratio were higher in patients with worse neurological stages compared to those in the early neurological stages ...

Larry Luxner, senior correspondent for Rare Disease Advisor (RDA), interviews cardiologist Pradeep P.A. Mammen, MD, of the University of Kansas School of Medicine, on the growing awareness of girls ...

CLL-related immune dysfunction, along with therapy-associated immunosuppression, contributes to impaired tumor surveillance. Patients with chronic lymphocytic leukemia (CLL) are at increased risk for ...

Adding antioxidants such as Trolox, Resveratrosl, and MitoTempo to the cooling regimen boosted the protection, even at higher temperatures, including 26°C. Hair loss due to the rigorous chemotherapy ...

The updated 2025 BSR management recommendations for patients with AAV provide systematic and evidence-based recommendations to support UK clinicians in managing AAV across the entire life course.

In addition to a 69.4% CR rate, the team observed good tolerability of the R2-MTX regimen, suggesting its suitability for older or less fit patients. High-dose methotrexate (HD-MTX) with lenalidomide ...

Relative survival increased from 64% to 66%, overall survival from 54% to 55%, and lymphoma-specific survival from 64% to 66%. The advent of chimeric antigen receptor T-cell (CAR-T) therapy for ...

(L-R) Rare Disease Advisor senior correspondent Larry Luxner, patient columnists Alithea Athans, Tara Keith and Tom Bartlett, and director of advocacy relations Vera Luxner (Photo by Riya Ajmera) ...

While I was sick with chronic inflammatory demyelinating polyneuropathy (CIDP), but before my diagnosis, my lack of sensation and proprioception had left me crawling around my apartment, wall walking, ...