Nusinersen - Wikipedia
Nusinersen, [7] marketed as Spinraza, [4] is a medication used in treating spinal muscular atrophy (SMA), a rare neuromuscular disorder. [8] [4] In December 2016, it became the first approved …
Nusinersen (Spinraza®) – Spinal Muscular Atrophy (SMA)
Nusinersen, marketed in the U.S. as Spinraza ® (Biogen) is the first therapy approved for the treatment of SMA. SMA results from mutations in a gene known as SMN1, which encodes a …
Official Patient Site | SPINRAZA® (nusinersen)
SPINRAZA ® (nusinersen) is a prescription medicine used to treat spinal muscular atrophy (SMA) in pediatric and adult patients. Increased risk of bleeding complications has been observed …
Nusinersen injection Uses, Side Effects & Warnings - Drugs.com
Sep 12, 2024 · Nusinersen works by helping the body produce a protein essential to the function of nerves that control muscle movement. This protein is lacking in people with an inherited …
SPINRAZA (nusinersen) injection, for intrathecal use . Initial U.S. Approval: 2016 _____ INDICATIONS AND USAGE _____ and as clinically needed. SPINRAZA is a survival motor …
FDA approves first drug for spinal muscular atrophy | FDA
FDA approved Spinraza (nusinersen), the first drug approved to treat children and adults with spinal muscular atrophy (SMA), a rare and often fatal genetic disease affecting muscle …
Nusinersen Injection: MedlinePlus Drug Information
Nusinersen injection is used for the treatment of spinal muscular atrophy (an inherited condition that reduces muscle strength and movement) in infants, children, and adults. Nusinersen …
Nusinersen (Spinraza) for Spinal Muscular Atrophy Treatment
One of the latest breakthroughs in care for patients with spinal muscular atrophy is the FDA approval of a new medicine called nusinersen (brand name Spinraza) for the treatment of …
Nusinersen: A Treatment for Spinal Muscular Atrophy
It is a novel modified antisense oligonucleotide designed to treat SMA caused by mutations in chromosome 5q that lead to survival motor neuron protein deficiency. Nusinersen has been …
The Antisense Oligonucleotide Nusinersen for Treatment of Spinal ...
An antisense oligonucleotide (ASO) drug, nusinersen, provides an upcoming and promising treatment option for SMA and represents a novel pharmacological approach with a mechanism …